AICD Prematurity Les paramètres respiratoires Icv ASO Adult patients Distal myopathy Antisense oligonucleotides ALS Dicer SMN Bone development Blood brain barrier CNS DPRs Maternal malnutrition Brain MRI Albumin gene targeting MRI Diseases Lentiviral vectors Spinal muscular atrophy ASOs Maternal behavior Fetal growth restriction Brain injury Inflammation FOXO3a Chondrocytes Brain development Clinical trials Brain Gene transfer Calcium handling MND Clinical markers Genetical therapy Microglia G-Secretase Biological marker MRNP assembly Maladie neuromusculaire Mecp2 Intra-CSF delivery Early-onset sepsis Cartilage and bone regeneration IPSCs Bone involvement FGR Duchenne Muscular Dystrophy Cell reprogramming Gene therapy Amyotrophic Lateral Sclerosis Genetics Errance diagnotique Cell stemness MUNIX C9orf72 Glucocorticosteroid Modèle murin Skeletal muscle 3xTgAD Mice MiRNA Long-term handicap Functional outcomes Melatonin Disease heterogeneity Adult SMA GABA LMNA DTI ERK1/2 signaling Biomarkers Cofilin-1 Neuromuscular disease Epigenetic changes Mouse model IRM Longitudinal progression CRISPR/SaCas9 GeneRide Brain imaging Bioinformatics Dilated cardiomyopathy Brain damage Adenosine Extremely preterm infants IUGR Effector T cells Fabry disease lysosomal storage disorders adeno asociated virus-9 Coagulation factor IX FTD Aav10 Intra-uterine growth restriction Clinical trial Disease modifiers Biomarker Cellules souches musculaires AAV Amyotrophie spinale