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Dernières publications
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Valentina Taglietti, Kaouthar Kefi, Lea Rivera, Oriane Bergiers, Nastasia Cardone, et al.. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine, 2023, 15 (685), ⟨10.1126/scitranslmed.add5275⟩. ⟨hal-04150315⟩
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A. Morin, Amalia Stantzou, Olga N. Petrova, John C.W. Hildyard, T. Tensorer, et al.. Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America, 2023, 120 (2), ⟨10.1073/pnas.2206324120⟩. ⟨hal-04122777⟩
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Valentina Taglietti, Kaouthar Kefi, Iwona Bronisz-Budzyńska, Busra Mirciloglu, Mathilde Rodrigues, et al.. Duchenne muscular dystrophy trajectory in R-DMDdel52 preclinical rat model identifies COMP as biomarker of fibrosis. Acta Neuropathologica Communications, 2022, 10 (1), ⟨10.1186/s40478-022-01355-2⟩. ⟨hal-03828280⟩
Chiffres clés
47
Publications avec texte intégral
Open Access
73 %
Mots clés
Cells
Dystrophie musculaire de Becker
NAD+
Drp1
Invivo
Liver
Centronuclear myopathy
Humans
LncRNA
Mitochondrial fission
Mdx mouse
L-Type
Allele‐specific silencing therapy
Cell Line
Male
Long noncoding RNA
Multi exon skipping
Clinical trials
Morphogenesis
Hear
Dystrophy
Ex-vivo
Molecular docking
Myogenesis
Skeletal muscle
Muscular Dystrophy
NNOS
Inhibitors
Human Umbilical Vein Endothelial Cells
Epigenetics
Base Sequence
Long QT
Dystrophin central domain
Cachexia
Animal/physiopathology
Activin Receptors
Genomic
Duchenne muscular dystrophy
Muscle Strength
Modificateurs de gènes
Myotendinous junction
Knockout
LKB1
Exon skipping
CaV subunits
Inbred mdx
Dystrophine
Dynamin 2
Molecular Sequence Data
LncARN
Dystrophin-EGFP
CTNNB1
Muscle
Metabolism
Becker muscular dystrophy
Gene modifiers
Hepatocellular carcinoma
Muscle Biology
Autophagy
Inbred C57BL
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
Calcium
Muscle development
Muscular Atrophy
Dystrophie Musculaire de Duchenne DMD
Calcium Channels
Delivery
CD38
Duchenne DMD dystrophy
Antisense oligonucleotides
Mice
Cultured
Becker BMD muscular dystrophy
Immunoglobulin Fc Fragments/pharmacology
Cardiomyopathie
DMO
Gene Expression Regulation/drug effects
Multi resolution modeling
Muscles/physiopathology
Homeostasis
Gene expression
Cell Biology
MiARN
Animals
DMD
Muscular dystrophy
MES
Dystrophin
BMD
CaVβs
Diseases
Energy Metabolism/drug effects
Génomique
Cell homeostasis
Duchenne muscular dystrophy DMD
Multiresolution modeling
Cardiomyopathy
Becker muscular dystrophy BMD
DHPR α1S
Dystrophie Musculaire de Becker BMD